FDA全球物质注册数据库(FDA Global Substance Registration System)
物质名称
NEXIGURAN
异名/同义词
NEXIGURAN NEXIGURAN [INN] NEXIGURAN [USAN] NTLA-2001 COMPONENT HU-G000480 RNA (SYNTHETIC HUMAN TRANSTHYRETIN GENE TTR-SPECIFIC SINGLE GUIDE G009979) RNA (SYNTHETIC HUMAN TRANSTHYRETIN GENE TTR-SPECIFIC SINGLE GUIDE) SINGLE-STRANDED GUIDE RNA (SGRNA) TARGETING THE HUMAN TRANSTHYRETIN (TTR) GENE WITH ITS 5'-TERMINAL 20 NUCLEOTIDES